FDA Approves First ALS Treatment Via Accelerated Approval
WEBApr 25, 2023 · ALS Association Funded Antisense Technology Behind Tofersen. Washington, D.C. (April 25. 2023) – The ALS Association commends the FDA for approving tofersen under the agency’s accelerated approval pathway for the treatment of people living with ALS connected to mutations in the SOD1 gene.
Phase 1 clinical trial of experimental ALS therapy ... - ALS News …
WEBAug 28, 2023 · Akava Therapeutics will soon launch a Phase 1 clinical trial to test AKV9, its investigational therapy for amyotrophic lateral sclerosis (ALS), in healthy people. The trial follows the clearance of Akava’s investigational new drug (IND) application by the U.S. Food and Drug Administration (FDA).
FDA final approval decision on NurOwn for ALS due by year’s end
WEBJun 8, 2023 · A final decision by the U.S. Food and Drug Administration (FDA) on whether or not to approve NurOwn for amyotrophic lateral sclerosis (ALS) is now expected no later than Dec. 8.
ALS News Today Home | ALS News Today
WEBSep 5, 2024 · Targeting 3 cell types at same time seen to extend survival in ALS mice. A strategy that simultaneously targets motor neurons, astrocytes, and microglia — three cell types involved in the development and progression of amyotrophic lateral sclerosis (ALS) — was shown to further extend survival in a mouse model of the disease.
Amyotrophic Lateral Sclerosis News -- ScienceDaily
WEBMar 13, 2024 · Latest research news on amyotrophic lateral sclerosis (ALS), also known as Lou Gehrig's disease, including experimental treatments.
News - The ALS Association
WEBStay up to date with the latest ALS news, with stories centered around research, care services, and advocacy.
Higher risk of ALS found for rare gene variants tied to Parkinson's
WEB4 days ago · The new study looked at genetic data from 791 people with a diagnosis of sporadic ALS in the Piedmont and Aosta Valley Registry for ALS (PARALS), a database that covers two regions in northwestern Italy, and 757 healthy people without the disease, who served as controls. Only patients with no known ALS-causing mutations were …
New studies point the way to broadly effective treatments for ALS
WEBFeb 7, 2023 · By leveraging a public bioinformatics database to identify how drugs affect the genetic landscape underpinning ALS, the scientists found that suppressing the SYF2 gene would increase the survival...
‘New’ ALS gene destabilizes neuron’s structure and chokes off its ...
WEBAug 18, 2023 · Northwestern Medicine scientists have discovered for the first time how this mutated gene leads to ALS (amyotrophic lateral sclerosis). The investigators found the mutation causes two problems in the neuron.
FDA approves controversial new drug designed to slow the progress of ALS
WEBSep 30, 2022 · The Food and Drug Administration on Thursday approved a new drug to slow the progression of ALS, a fatal neurodegenerative disease for which there is no cure.
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