A new approach... Lucy Landman was born with a very rare genetic disorder that causes severe intellectual disability, weak muscles and seizures, among other symptoms. "She is expected to very much ...

and developing therapies for rare pediatric genetic diseases. In collaboration with 15 centres across India, CDFD is recruiting patients and their families to participate in this study.

Lucy Landman was born with a very rare ... from one disease to another and not take four years and $10 million to do that,“ Urnov says. The approach from one patient to the next would be essentially ...