University of Wisconsin–Madison researchers targeting a group of hereditary neurodegenerative diseases have found success ...

A Michigan State University researcher's new model for studying breast cancer could help scientists better understand why and ...

Sep. 9, 2024 — Researchers tested a preclinical model for an experimental gene therapy designed to treat multiple sulfatase deficiency (MSD), a disorder that affects the brain, lungs ...

Cardiovascular disease remains the foremost cause of morbidity and mortality globally, affecting millions of individuals. Recent discoveries illuminate the substantial role of genetics in ...

Researcher creates a groundbreaking genetic model for breast cancer, offering new insights and potential advances in ...

Professor Eran Andrechek who teaches in the MSU Department of Physiology, has been researching the E2F5 gene, of which little ...

Neurogene's stock price collapsed by 34.8% in pre-market trading after announcing data from the Phase I/II Rett syndrome ...

New legislation would clarify rules around value-based contracts in Medicaid, and a new model is expanding access to gene therapies, explained Adam Colborn, JD, of AMCP.

In-depth interviews and an online survey found support for gene therapy as a treatment for inherited blood disorders, but ...

Its pipeline targets Mendelian disorders, precision oncology, and gene therapy, with four programs in late-stage ... After reviewing our model, we now forecast a slow ramp-up of sales for acoramidis ...

Neurogene has a $903M market cap with two phase 1/2 assets, NGN-401 for Rett Syndrome and NGN-101 for CLN5 Batten Disease.

University of Wisconsin-Madison researchers targeting a group of hereditary neurodegenerative diseases have found success ...