Stem cells can tailor their role in gene therapy based on the underlying disease, study suggests
RCCS San Raffaele Scientific Institute in Milan researchers have discovered that hematopoietic stem cells (HSCs) adapt their lineage commitment during gene therapy based on the underlying genetic ...
University of Pennsylvania gene therapy spinout Interius BioTherapeutics doses patient, achieves CAR therapy first
Its lead gene therapy candidate has the potential to be faster, less expensive, and more widely available than current CAR T ...
Baylor College of Medicine4d
Grants awarded to leading investigators at Baylor's Center for Cell and Gene Therapy
Three investigators at Baylor College of Medicine’s (BCM) Center for Cell and Gene Therapy Institute (CAGT ... received a $100,000 G-Rex Grant to develop a novel G-Rex based approach for culturing ...
Becker's Hospital Review3d
Sickle cell patient dies in gene-therapy trial
Beam Therapeutics' early clinical data shows promising results for sickle cell disease treatment using CRISPR gene editing tool. One patient died ...
GEN3d
Hospital-Based CGT Production the Best Option for Patients
In-house manufacturing in a GMP facility of a hospital represents a centralized approach to manufacturing that secures ...
Managed Healthcare Executive9d
Managed Care Experts Agree on Gene Therapy’s Clinical Benefits for Inherited Blood Disorders But See Hurdles for Coverage
In-depth interviews and an online survey found support for gene therapy as a treatment for inherited blood disorders, but ...
labiotech3d
Cystic fibrosis: Five biotechs breathing life into the therapeutic space
In this article, we take a look at five biotech companies developing potentially transformative medicines to treat cystic ...
labiotech5d
Unlocking AAV gene therapy potential: The role of successful characterization
Explore the role and challenges of AAV characterization, the significance of capsid filling, and the best methods to enhance gene therapy.
News Medical on MSN12d
Researchers uncover key mechanisms of CRISPR gene editing
CRISPR/Cas9 is a gene editing tool that has revolutionized biomedical research and led to the first FDA-approved CRISPR-based gene therapy.
The American Journal of Managed Care7d
Medicaid Aiming to Improve Patient Access to High-Cost Therapies
New legislation would clarify rules around value-based contracts in Medicaid, and a new model is expanding access to gene therapies, explained Adam Colborn, JD, of AMCP.