Children with spinal muscular atrophy (SMA) experience benefits from receiving a disease-modifying gene therapy, but many ...

Jenssen guessed then that two of her daughters, the twins, had a Duchenne mutation, and she knew in her heart that, for at ...

Imperial to join ATTC NetworkImperial has joined the Advanced Therapies Treatment Centre (ATTC) Network which aims to accelerate the delivery of cell ...

Queen Mary University of London is delighted to be a part of the new London-based Advanced Therapy Treatment Centre (ATTC).

Rocket Pharmaceuticals announced enrollment completion for phase 2 study using its gene therapy RP-A501 for treatment of male ...

It’s been almost a year since the Food and Drug Administration approved the first genetic treatments for sickle cell disease.

gene editing, cell engineering and machine learning to overcome the development and scaling complexities associated with cell therapy and improve patient access across a broad range of disease areas.

Penn gene therapy pioneer Dr. Jim Wilson said his decision to leave academia to become full-time CEO of two startups he ...

Age-related musculoskeletal diseases are a significant public health concern that critically impacts the motor functions and the quality of life in the elderly. The musculoskeletal system supports the ...

Just a few months after the reveal of Ori Biotech’s automated cell and gene therapy manufacturing platform IRO, the technical ...

Having already scooped up the U.S. rights to Capricor Therapeutics’ late-stage Duchenne muscular dystrophy (DMD) therapy, ...

The MACC Fund Center for Cancer and Blood Disorders at Children’s Wisconsin is now offering a new gene therapy to children ...