Children with spinal muscular atrophy (SMA) experience benefits from receiving a disease-modifying gene therapy, but many ...

Jenssen guessed then that two of her daughters, the twins, had a Duchenne mutation, and she knew in her heart that, for at ...

FN Media Group News Commentary - Breast cancer is an illness in which the breast cells get uncontrollably large. The type of breast cancer depends on which cells in the breast become cancerous. Cancer ...

For people with SCD, hemoglobin S (a mutated protein that transports oxygen) causes red blood cells to become curved ...

Rocket Pharmaceuticals announced enrollment completion for phase 2 study using its gene therapy RP-A501 for treatment of male ...

Shares dropped by as much as one-quarter Thursday after the biotech shared longer-term results for a gene therapy it’s developing for wet AMD.

The Gene Therapy segment focuses on the gene therapy approach to introduce ... using small drug molecules that bind to the melanocortin receptors on human cells and affect skin pigmentation and other ...

There are several other gene therapies being studied that are ... including medications, physical therapy and sometimes nerve blocks. — Pulmonologists. Sickle cell disease can lead to lung ...

It’s been almost a year since the Food and Drug Administration approved the first genetic treatments for sickle cell disease.

GC Therapeutics has entered gameplay with the mission of unlocking a new generation of cell therapies, uploading with $75 ...

gene editing, cell engineering and machine learning to overcome the development and scaling complexities associated with cell therapy and improve patient access across a broad range of disease areas.

Cancer, as we all know, happens when there’s a change in or damage to genes in cells, which then cannot function normally ... to pave the way for precision and personalized medicine. What is precision ...