Cure” is a not an immutable term, the authors of a new study write, and its meaning depends on the context in which it is ...

Children with spinal muscular atrophy (SMA) experience benefits from receiving a disease-modifying gene therapy, but many ...

"First cohort benefits from Atsena Therapeutics XLRS gene therapy" was originally created and published by Clinical Trials Arena, a GlobalData owned brand. The information on this site has been ...

This new economic valuation of the societal and health care benefits of gene therapy to treat sickle cell disease (SCD) concludes the highly personalized treatment has potential to be cost ...

D Molecular Therapeutics reported its experimental gene therapy demonstrated a nearly 90% reduction in the need for ...

The first therapy that uses gene-editing is to be offered on the NHS in a “revolutionary breakthrough” for patients. It will ...

A team of researchers report findings from a Phase I/II gene therapy clinical trial for patients with Leber congenital ...

He also believes there’s still too few of the therapies on the market to draw any sweeping conclusions on reasons for their ...

A newly developed gene therapy shows great potential for treating glaucoma, a condition that can lead to vision loss.

Just a few months after the reveal of Ori Biotech’s automated cell and gene therapy manufacturing platform IRO, the technical ...

Ori Biotech (Ori), a leader in cell and gene therapy (CGT) manufacturing enabling technology, and Charles River Laboratories (Charles River), a global industry-leading drug discovery, preclinical ...

Unfortunately, gene therapy is not this simple ... These include matters related to weighing potential harms and benefits, establishment of procedural fairness in selection of patients for ...