Subsequently, it leads to deformed blood cells that adopt a crescent shape that looks like a sickle under a microscope. 2 CRISPR Cas9: Gene Therapy Play The rigid, distorted red blood cells cause ...

For now, gene-editing interventions are so complex and costly that only people in wealthy countries are receiving them. The first such therapy to get FDA approval, a treatment for sickle-cell ...

Newly appointed CMO, Dr. Emmanuelle Dochy, and newly appointed CSO, Dr. Maurizio Ceppi, bring a strong track record of advancing cancer ...

BT-001 monotherapy showed stable disease and shrinkage of injected lesions in patients with advanced solid tumors. BT-001 in combination with ...

Mice treated with the gene therapy remained cancer-free for at least 100 days and resisted cancer resurgence in a lab test.

It’s been almost a year since the Food and Drug Administration approved the first genetic treatments for sickle cell disease.

Advancements in cell and gene therapy have been driven by improved insights into the human immune system and a better ...

There's new hope for people with sickle cell disease which affects mainly African Americans. It's gene therapy research at ...

Kendric Cromer undergoing infusion gene therapy for his sickle cell disease at Children’s National Hospital in Washington last week.Credit...Kenny Holston/The New York Times Supported by By Gina ...